Ultragenyx Pharmaceutical
Pharmaceutical / Biotechnology
Companies / Ultragenyx Pharmaceutical
0
Latest Hiring Jobs
5
Clinical Trials
0
FDA Products
0
Publications
Company Overview
COMPANY TYPE
Unknown
INDUSTRIES
Unknown
HEADQUARTERS
WEBSITE
Not available
Clinical activity detected
This company has 7 clinical trial records in the intelligence database.
Clinical Development
Recent clinical trial activity
7 Trials
Trial Phase Status Enrollment Start Date Condition
NCT02971969
Long-Term Safety, Tolerability, and Efficacy of DTX101 (AAVrh10FIX) in Adults With Moderate/Severe to Severe Hemophilia B
Observational COMPLETED - - Hemophilia B
NCT07447648
Assessing the Impact of Intensification of Lipid Lowering Therapy With Guidelines-based Evinacumab Administration on Coronary Plaque Volumes Measured by Coronary Computed Tomography Angiography (CCTA) in Patients With Homozygous Familial Hypercholesterolemia (HoFH)
Observational RECRUITING - - Homozygous Familial Hypercholesterolemia (HoFH), Coronary Computed Tomography Angiography
NCT07159581
Gene Therapy for Wilson Disease Evaluated by 64Cu PET/CT
Observational ENROLLING BY INVITATION - - Wilson Disease
NCT04909346
Adeno-Associated Virus (AAV) Antibody Study in Subjects OTC Deficiency, GSDIa, and Wilson Disease
Observational TERMINATED - - Ornithine Transcarbamylase Deficiency, Wilson Disease
NCT02931682
Observational Study of Males With Creatine Transporter Deficiency
Observational TERMINATED - - Creatine Deficiency, X-linked
Company Intelligence
Company profile enrichment is not available yet.

Hiring Intelligence

Latest open positions detected for this company
View All Jobs
No current hiring positions found.
FDA Regulatory Intelligence
FDA product and regulatory signals
0 Signals
No FDA regulatory data available.